Outcome Measures to Assess Curative Therapy

For select webcasts and other resources from the WFH 2018 World Congress go to:

In the Wednesday afternoon session entitled Past, Present, and Future of Gene Therapy: From Vectors and Transgenes to Outcomes, Alfonso Iorio discusses different efficacy and safety outcome measurements, particularly in the context of the coreHEM definition of the core outcome set for gene therapy in hemophilia.

World Federation of Hemophilia,Alfonso Iorio,